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Beam presents new NHP data demonstrating proof-of-concept for ESCAPE
durable production of fetal hemoglobin in a non-human primate model. ESCAPE is comprised of two investigational drug products: BEAM-103, an anti-CD117 monoclonal antibody that is designed to ...
Nature6d
Fetal Hemoglobin Bart's Disease and Prenatal Diagnosis
Fetal Hemoglobin Bart's Disease is a severe form of alpha thalassemia that can lead to significant complications during pregnancy, including fetal anemia and hypoxia. This condition arises from ...
Yahoo Finance9d
YolTech Therapeutics to Initiate a Clinical Trial for YOLT-204, a First-in-Class Bone Marrow-Targeted In Vivo Gene Editing Therapy for β-Thalassemia
The therapy edits the regulatory region of hemoglobin to induce expression of fetal hemoglobin, potentially alleviating the imbalance of hemoglobin production and normalizing the number of red ...
Mena FN9d
Yoltech Therapeutics To Initiate A Clinical Trial For YOLT-204, A First-In-Class Bone Marrow-Targeted In Vivo Gene Editing Therapy For Î’-Thalassemia
The therapy edits the regulatory region of hemoglobin to induce expression of fetal hemoglobin, potentially alleviating the imbalance of hemoglobin production and normalizing the number of red ...