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'Will it really work?': Young sickle cell patient among the first to start new gene therapy
D.C., for his stem cell collection — the first major step of the revolutionary sickle cell gene therapy process. “But that ...
GoodNewsNetwork1d
New Base Editing Gene Therapy Cures its First Patient: A Sickle-Cell Sufferer Now in the ‘Gym Every Day’
Base editing utilizes enzymes to modify single amino acids at the most foundational unit of DNA, called a base.
Health Affairs2d
Beyond Gene Therapies: People With Sickle Cell Disease Need Comprehensive Care
We can do better. We can build a system that provides coordinated high-quality care to every patient who needs it.
Beam Therapeutics: Too Expensive For Me, But Watch For Important Catalysts
Beam Therapeutics shows promise in gene therapy for sickle cell disease, but it also has high risks and market expectations.
gh.bmj2d
Strengthening advanced therapy for sickle cell disease in Africa: experience from sickle cell disease centre in Dar es Salaam, Tanzania
Despite progress in healthcare services for individuals living with sickle cell disease (SCD) in Africa, substantial gaps ...
BioSpace7d
WHO Withdrawal, CGT Access, IRA: Trump’s Initial Policies Raise Questions for Biopharma
At J.P. Morgan, most biopharma executives expressed a neutral stance on the incoming administration, but just days later, ...
Becker's Hospital Review2d
Children's Hospital Los Angeles adds sickle cell treatment
Discover the latest addition to Children's Hospital Los Angeles' 10 cell and gene therapy treatments, including Casgevy for sickle cell disease ...
Employee Benefit News8dOpinion
Why costly gene therapy is top of mind for benefits administrators
Whether or not to cover these procedures, and if so, coverage details, should be decided on before their popularity grows.
HHS Challenges Vertex Over Fertility Services Program Tied To Casgevy Gene Therapy, Says Company Is 'Grasping at Straws'
HHS challenges Vertex Pharmaceuticals' fertility services program, alleging violations of anti-kickback laws linked to its ...
NBC News11d
'Will it really work?': Young sickle cell patient among the first to start new gene therapy
“You are one of the few in the country and even in the world, you know, taking this big step — gene therapy,” said Campbell, director of the hospital’s Comprehensive Sickle Cell Disease ...