StarsInsider on MSN22h
What do we know about tuberous sclerosis?
Tuberous sclerosis, also called tuberous sclerosis complex (TSC), is a rare genetic multisystem disorder characterized by the ...
Agios Pharmaceuticals: Considering Risk/Reward Ahead Of FDA Decision
Agios Pharma submitted a sNDA to the FDA after two Phase III trials studying PYRUKYND (mitapivat) in thalassemia met their ...
Rising Incidence and Newborn Screening Programs Spur Rapid Growth in Sickle Cell Anemia Diagnostics
Asia Pacific Leads Next Wave of Sickle Cell Screening Adoption as Public Health Funding Expands Global Sickle Cell Anemia ...