BioPharma Dive19h
Sickle cell patient dies in Beam study of base editing therapy
Beam’s medicine uses a technology known as base editing to activate a gene in stem cells collected from people with sickle ...
A sickle cell cure exists. But patients need more than just gene therapy.
Almost a year after two historic approvals, Pfizer is pulling a sickle cell disease treatment from the market, and the ...
sicklecellanemianews5d
Oral AND017 granted orphan drug status for SCD
The FDA granted orphan drug status to Kind Pharmaceuticals' investigational oral small molecule AND017 to treat SCD.
Pfizer CEO Defends Turnaround Strategy as Activist Pressures Management
(Reuters) -Pfizer CEO Albert Bourla, under pressure from activist hedge fund Starboard Value, made his case to Wall Street on Tuesday that the drugmaker's turnaround is succeeding after it reported a ...